Duchenne Muscular Dystrophy Market Growth, Share, Size & ForecastA Story by Bhuwan SinghThis is mainly because expanding treatment options will give patients access to a broader range of treatment options, enabling growth and penetration in the Duchenne Muscular Dystrophy industry as morAccording to a new report by UnivDatos Market Insights, the Duchenne Muscular Dystrophy Marketreached USD 800 million in 2023 and will grow at a CAGR of ~7% during the year 2024-32F. This is mainly because expanding treatment options will give patients access to a broader range of treatment options, enabling growth and penetration in the Duchenne Muscular Dystrophy industry as more therapies receive regulatory approval. For instance, on March 21, 2024, the U.S. Food and Drug Administration approved Duvyzat (givinostat) oral medication for treating Duchenne Muscular Dystrophy (DMD) in patients six and older. Duvyzat is the first nonsteroidal drug approved to treat patients with all genetic variants of DMD. This expansion will enhance personalized care approaches, allowing for better disease management based on individual patient needs. The ability to
tailor treatments to individual genetic profiles and specific disease
manifestations enhances patient outcomes and drives market demand. Some of the
key developments influencing the Duchenne Muscular Dystrophy market include: ·
On
March 28, 2024, Critical
Path Institute’s (C-Path) Duchenne Regulatory Science Consortium (D-RSC)
announced the launch of a groundbreaking model-based Clinical Trial Simulator
(CTS) specifically designed to improve the design of efficacy studies for
potential therapies for Duchenne muscular dystrophy (DMD). This pioneering Drug
Development Tool is set to positively impact the medical research community by
significantly optimizing clinical trial design. ·
On
January 5, 2023,
Sarepta Therapeutics announced the signing of a commercial supply agreement for
Catalent to manufacture delandistrogene moxeparvovec (SRP-9001), Sarepta’s most
advanced gene therapy candidate for the treatment of Duchenne muscular
dystrophy (DMD). ·
On
September 30, 2022, Solid
Biosciences Inc., a life sciences company focused on advancing meaningful
therapies for Duchenne muscular dystrophy (Duchenne), announced the closing of
its acquisition of AavantiBio, Inc., a privately held gene therapy company
focused on transforming the lives of patients with Friedreich’s ataxia and rare
cardiomyopathies. The acquisition included its pipeline assets and net cash. The regulatory framework's focus on
personalized medicine has led to the approval of treatments tailored to individual
needs and desired outcomes, enhancing patient satisfaction and driving market
demand. Some of the most approved treatments for Duchenne Muscular Dystrophy
include: The treatment of Duchenne muscular
dystrophy has included significant non-steroidal advances that offer new hope
for managing the disease. Among these, Duvyzat (givinostat) stands out as a
noteworthy development. Approved by the FDA in March 2024, Duvyzat is a
non-steroidal histone deacetylase (HDAC) inhibitor that has demonstrated
efficacy in reducing muscle deterioration across all genetic forms of Duchenne
muscular dystrophy. ·
On
June 22, 2023,
Sarepta Therapeutics announced U.S. Food and Drug Administration (FDA)
accelerated approval of ELEVIDYS, an adeno-associated virus-based gene therapy
for the treatment of ambulatory pediatric patients aged 4 through 5 years with
Duchenne muscular dystrophy (DMD) with a confirmed mutation in the DMD gene. Conclusion In conclusion, the Duchenne Muscular
Dystrophy (DMD) market is poised for substantial growth, fueled by increasing
prevalence, innovative therapies, and a supportive regulatory landscape. With a
projected CAGR of ~7% from 2024 to 2032, the market registered USD 800 million in
2023. The market is witnessing significant advancements, such as the approval
of Duvyzat and ELEVIDYS, marking a shift towards personalized medicine.
Moreover, initiatives like the launch of the Clinical Trial Simulator and
strategic agreements between companies further indicate a promising future for
DMD treatment development and patient care. Contact Us: © 2024 Bhuwan Singh |
Stats
60 Views
Added on June 27, 2024 Last Updated on June 27, 2024 Tags: Duchenne Muscular Dystrophy Mark Author
|